6 Year Old Saffie Has Her Vision Saved from Rare Form of Blindness Thanks to One-Time Gene Therapy

A 6-year-old girl in the UK is able to see normally again in the day and night thanks to a one-time gene therapy for a rare form of congenital blindness. At this very tender age, Saffie Sandford from Stevenage was diagnosed with Leber's Congenital Amaurosis, (LCA) a mutation in the RPE 65 gene which both