New Treatment Shows Remarkable Motor Improvements in Boys With Muscular Dystrophy—in Just 12 Weeks

Scientists studying one of the world's most serious inherited muscle diseases have found encouraging evidence that treating children much earlier—potentially before obvious symptoms develop—could make a significant difference. Researchers at Binghamton University in New York are studying the drug Vamorolone in very young boys with Duchenne muscular dystrophy (DMD), a progressive genetic disorder that causes